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Titel:

Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines.

Dokumenttyp:
Journal Article; Review
Autor(en):
Peters, C; Steward, CG
Abstract:
For the past two decades, hematopoietic cell transplantation (HCT) has been used as effective therapy for selected inherited metabolic diseases (IMD) including Hurler (MPS IH) and Maroteaux-Lamy (MPS VI) syndromes, childhood-onset cerebral X-linked adrenoleukodystrophy (X-ALD), globoid-cell leukodystrophy (GLD), metachromatic leukodystrophy (MLD), alpha-mannosidosis, osteopetrosis, and others. Careful pre-HCT evaluation is critical and coordinated, multidisciplinary follow-up is essential in thi...     »
Zeitschriftentitel:
Bone Marrow Transplant
Jahr:
2003
Band / Volume:
31
Heft / Issue:
4
Seitenangaben Beitrag:
229-39
Sprache:
eng
Volltext / DOI:
doi:10.1038/sj.bmt.1703839
PubMed:
http://view.ncbi.nlm.nih.gov/pubmed/12621457
Print-ISSN:
0268-3369
TUM Einrichtung:
Klinik und Poliklinik für Kinderheilkunde und Jugendmedizin
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