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Title:

Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study

Document type:
Zeitschriftenaufsatz
Author(s):
Pechmann, Astrid ; Behrens, Max ; Dörnbrack, Katharina ; Tassoni, Adrian ; Wenzel, Franziska ; Stein, Sabine ; Vogt, Sibylle ; Zöller, Daniela ; Bernert, Günther ; Hagenacker, Tim ; Schara-Schmidt, Ulrike ; Walter, Maggie C. ; Bertsche, Astrid ; Vill, Katharina ; Baumann, Matthias ; Baumgartner, Manuela ; Cordts, Isabell ; Eisenkölbl, Astrid ; Flotats-Bastardas, Marina ; Friese, Johannes ; Günther, René ; Hahn, Andreas ; Horber, Veronka ; Husain, Ralf A. ; Illsinger, Sabi...     »
Keywords:
Research ; Pediatric neuromuscular diseases ; Spinal muscular atrophy ; Nusinersen ; Sitter ; Later-onset ; SMArtCARE ; Medical and Health Sciences
Journal title:
Orphanet Journal of Rare Diseases
Year:
2022
Journal volume:
17
Journal issue:
1
Fulltext / DOI:
doi:10.1186/s13023-022-02547-8
Publisher:
BioMed Central
E-ISSN:
1750-1172
Date of publication:
23.10.2022
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